This is a question many people asking about the Covid-19 vaccine considering it was approved so quickly. MHRA chief executive explains the process in the article below to reassure.
We had a special guest at TreatSMA today, Santa Claus asked to speak to everybody via video conference to share a message to us all. This was live on Facebook but for those who do not follow us on social…
We are really excited and pleased to inform you that our very own Trustee, Andi, who has SMA type 2 has been chosen to sit on the panel for NICE appraisal of Risdiplam. Andi will be the first adult with…
As you know our mission is treatment for all, and we have continued this fight by exposing Cambridge University Hospitals of their continued age discrimination against those with Spinal Muscular Atrophy. Equal access to health is the very tenant of the NHS yet CUH seem to feel otherwise.
Cambridge University Hospitals (CUH) is regarded as one of the most reputable medical institutions worldwide and provides specialist services to many conditions nationally and internationally, including being a Neuromuscular Centre of Excellence as awarded by MDUK. Therefore, it begs the question, why, when the FDA, MHRA and most other Neuromuscular Centres across the country are prescribing risdiplam to patients of all ages, does CUH feel able to have a different opinion to all of these experts?
If NICE recommends next year that England’s Managed Access Agreement for nusinersen should change to include you / your child, would you want to access this treatment?
In this session Marion talks about all of the different ways you can use that you can use different types of equipment for different types of exercise.