The SUNFISH clinical trial is progressing fast, and all of its planned 186 participants will likely be recruited in the next few weeks. As of last week, enrollment of participants aged 6–11 and 18–25 years has been completed globally. However, nobody in the UK in those age groups will participate in this long-awaited trial as the all-too-prevalent red tape has impeded the opening of UK trial sites.
On 27 June 2018, NICE Appraisal Committee will meet in Manchester to discuss draft recommendation for Spinraza provision in England and Wales. Parts of the meeting will be open to the public and you are welcome join.
Today Roche announced they decision to stop the development of olesoxime, a neuroprotective drug that showed benefit in spinal muscular atrophy. Below is their statement: