Today a group of TreatSMA families attended a meeting of the All-Party Parliamentary Group for Muscular Dystrophy at the House of Lords.
First ever treatment for life-devastating condition is approved by European Commission!
On the 19th of May, Biogen attended a meeting arranged between 4 patient advocacy groups: Muscular Dystrophy UK, SMA Trust, SMA Support UK and TreatSMA.
EAP started/starting Newcastle Belfast East Dundee Great Ormond Street Oxford Evelina Leeds Liverpool Glasgow Bristol Cardiff Sheffield (August) Working towards EAP Cambridge Birmingham Oswestry Manchester We're still waiting on responses from St George's (London) Contacts we have Evelina Childern's Hospital: Dr…
EMA Committee adopted a positive opinion on Spinraza!
Biogen announced that the Expanded Access Programme for nusinersen will not be extended to SMA types 2 and 3.
Every month, across the UK, parents are hearing the devastating words from doctors that their baby is extremely unlikely to survive to see their 2nd birthday. That they will helplessly be forced to watch as their baby grows weaker before their…