Health authorities in Turkey decided to offer Spinraza as a standard therapy to all people with spinal muscular atrophy.
MP drop-in, House of Commons on 25th February 2019
On Tuesday the 26th the TreatSMA team met the new generation and talked about living with rare diseases like SMA.
Irish families will once again march on the Dáil this Thursday 28th February to demand the Health Service Executive approve Spinraza NOW.
Spinraza has been called the most high-profile case of “inflexible, inappropriate” approach by NICE to some rare disease drugs in a newly published analysis.