skip to Main Content

What a community! Thank you.

  • 30 October 2020

Today TreatSMA made submissions to NICE to help with the appraisal of Risdiplam to be made available through NHS. We have included extensive data collected from community (over 300 responses in total, so massive thank you).

Read More

EAMS update and how you can help

  • 21 October 2020

You may remember some time ago we posted that MHRA had approved an EAMS process for accessing risdiplam. Just to remind everybody what an EAMS process is, it stands for Early Access to Medicines Scheme, and is designed to provide those who currently have unmet clinical needs to get access to life-saving treatment before it is licensed in the UK.

Read More
Back To Top