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NICE refuses to recommend Spinraza to treat SMA

  • 14 August 2018

In the draft guidance issued today, the National Institute of Health and Care Excellence (NICE) decided NOT to recommend the use of nusinersen (Spinraza®) as an NHS treatment for spinal muscular atrophy in England and Wales.

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AveXis gene therapy trial in UK

  • 10 August 2018

In the next few weeks we are expecting the AveXis AVXS-101 trial to start enrolling. There will be two site centres here in the UK: Great Ormond Street Hospital for Children Contact : [email protected] The John Walton Muscular Dystrophy Research…

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Adapted Trikes

  • 6 August 2018

Please note this is not an affiliated Theraplay post, this is a review compiled by an owner of an adapted trike who has no association to the company and the views are their own. Adapted trikes are a great way…

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August is SMA Awareness Month

  • 1 August 2018

It's August and its SMA Awareness Month. Please take time to view and share our video. Lets TreatSMA in all its forms, and lets get more treatments as soon as we can to help all.

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