Campaign for Access to Treatments for Spinal Muscular Atrophy

We have received notification that the Physical ability: What is important to you? The study has reached its quota for non-ambulant participants. As well as this they have extended the age range to 2-60 years old. Therefore, please see updated invitation below:

Are you interested in participating in two telephone/video interviews to discuss your experience of Spinal Muscular Atrophy (SMA) and to help us understand what an important change in physical ability would be?

Today Biogen provided us with an update on the NURTURE study which was published in Muscle & Nerve¹.

Scholar Rock have announced new 36-Month Apitegromab Extension Data which reinforces long-term substantial and sustained improvement of motor function in phase 2 Topaz trial patients with Nonambulatory SMA.

On Wednesday 12th July 2023, 7pm to 8pm the National Institute for Health and Care Research, which supports delivery of research in the NHS, public health and social care and Muscular Dystrophy UK, the UK charity for individuals and families living…

Are you interested in participating in two telephone/video interviews to discuss your experience of Spinal Muscular Atrophy (SMA) and to help us understand what an important change in physical ability would be?

Google Maps is providing wheelchair accessibility information by default for over 40 million places worldwide, including on public transport, pubs and restaurants. The feature can help those with mobility needs to plan their trips by checking if the shop or landmark they’re…

Disability Expo esteemed panel of experts are bringing a diverse perspective and shedding light on the challenges, triumphs, and unique experiences faced by individuals with disabilities in navigating their sexual and relational lives this Thursday 25th May at 1pm GMT.…

Skiggle offer support for disabled individuals, by funding and operating a unique round-the-clock SOS emergency alert service. This provides a place for people to turn to if they urgently need a piece of equipment, feed, or disability care product.