As we published earlier in the week TreatSMA is proud to be supporting the Royal Holloway’s 10th Annual Rare Disease Day Event on Wednesday 26th in support of Rare Disease Day. However, the excitement doesn’t stop there.
TreatSMA hosted another Physio with Marion session on Sunday, and thanks to Marion and all of those who took part in asking questions, his week’s session focused on standing and walking and there were lots of great questions.
TreatSMA are proud to announce that we will be one of the sponsors for Royal Holloway’s 10th Annual Rare Disease Day Event on Wednesday 26th of February.
Roche released part 2 of the SUNFISH data which shows significant improvement both type 2 and type 3 patients. Read on for further details.
TreatSMA hosted another Physio with Marion session on Sunday, and thanks to Marion and all of those who took part in asking questions, it was another great success which saw questions and views from around the globe.
Today Roche announced that it is making risdiplam available through a global Pre-Approval Access/Compassionate Use Programme. Under the programme, the company will provide risdiplam for patients who cannot receive an approved treatment.